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Laminopathies
Amyotrophic lateral sclerosis
LMNA
Regeneration
AAV
Duchenne muscular dystrophy
Lamin A/C
Rare neuromuscular diseases
Cell therapy
Satellite cell
PABPN1
Glutamate
Congenital myopathy
Centronuclear myopathy
Dermatomyositis
LMNA gene
Dynamin 2
Myasthenia gravis
Myoblasts
Muscle regeneration
Long read sequencing
Myopathy
Animals
Treatment
Cardiomyopathy
CMS
Biomarker
Autoimmune diseases
Neuromuscular junction
Heart failure
Dystrophin
Myopathies
Mechanotransduction
Neuromuscular diseases
CRISPRi
Actin
Diagnosis
Skeletal muscle
RNA interference
Therapy
Becker muscular dystrophy
Genotype phenotype correlation
Exercise
Errance diagnostique
Antisense oligonucleotides
Outcome measures
Calcium
FSHD
Alternative splicing
Humans
DMD
RNA biology
Transcriptomics
Heart
ALS
Inflammation
Laminopathy
Myasthenia Gravis MG
Transgenic mouse model
Cytokines
Myotonic dystrophy type 1
Dilated cardiomyopathy
Myogenesis
Trinucleotide repeat expansion
Thymus
Cancer
Laminopathie
Mouse model
Neuromuscular disease
Astrocyte
Myositis
Brain
Biomarkers
Cytoskeleton
CTG repeat contractions
Thérapie génique
COVID-19
Aged
Lamin A/C LMNA gene
MBNL
Myotonic Dystrophy type 1
Autoantibodies
Fibrosis
Myotonic dystrophy
Aging
Muscle
Clinical trials
Rare diseases
OPMD
Myotonic Dystrophy
Gene therapy
Satellite cells
Fabry disease
Autophagy
Congenital muscular dystrophy
Autoimmunity
Male
Nuclear envelope
Motoneuron
Muscular dystrophy